Lessons for future clinical trials in adults with Becker muscular dystrophy: Disease progression detected by muscle magnetic resonance imaging, clinical and patient-reported outcome measures.

Auteurs

De Wel B, Iterbeke L, Huysmans L, Peeters R, Goosens V, Dubuisson N, van den Bergh P, Van Parijs V, Remiche G, De Waele L, Maes F, Dupont P, Claeys KG

  • Date de publication

    March 2024
  • Type

    Article
  • Review

    Eur J Neurol
  • Researcher's name

    Remiche Gauthier
  • Hôpital

    Hôpital Erasme
  • Service

    Neurologie
  • PMID

    38504654
  • DOI

    10.1111/ene.16282