Improvements in Health-Related Quality of Life in Patients with Severe Sickle Cell Disease After Exagamglogene Autotemcel.

Auteurs

Sharma A, Locatelli F, Bhatia M, Molinari L, Mapara MY, Liem RI, Dedeken L, Wall D, Eckrich MJ, Kuo KHM, Smith W, Imren S, Kohli P, Li N, Liu T, Rubin J, Hobbs WE, Grupp SA, Frangoul H

  • Date de publication

    August 2025
  • Type

    Article
  • Review

    Blood Adv
  • Researcher's name

    DEDEKEN Laurence
  • Hôpital

    Hôpital Universitaire des Enfants
  • Service

    Clinique d'Hématologie pédiatrique bénigne
  • PMID

    40857358
  • DOI

    10.1182/bloodadvances.2025016701